Cure models have been developed as an alternative modelling approach to conventional survival analysis in order to account for the presence of cured subjects that will never experience the event of interest. Mixture cure models, which model separately the cure probability and the survival of uncured subjects depending on a set of covariates, are particularly useful for distinguishing curative from life-prolonging effects. In practice, it is common to assume a parametric model for the cure probability and a semiparametric model for the survival of the susceptibles. Because of the latent cure status, maximum likelihood estimation is performed by means of the iterative EM algorithm. Here, we focus on the cure probabilities and propose a two-step procedure to improve upon the performance of the maximum likelihood estimator when the sample size is not large. The new method is based on the idea of presmoothing by first constructing a nonparametric estimator and then projecting it into the desired parametric class. We investigate the theoretical properties of the resulting estimator and show through an extensive simulation study for the logistic-Cox model that it outperforms the existing method. Practical use of the method is illustrated through two melanoma datasets.
翻译:作为常规生存分析的一种替代建模方法,已经开发了昆虫模型,作为常规生存分析的一种替代建模方法,以便考虑到治疗对象的存在情况,这些对象永远不会受到关注; 混合治愈模型,这些模型根据一组共变体分别作为治愈概率和未治愈对象存活率的模型,对于区分治疗与寿命延长效应特别有用; 在实践中,通常的做法是假设治愈概率的参数模型和受感染者生存的半参数模型; 由于潜在治愈状态,因此通过迭代EM算法进行最大可能性估计。 这里,我们侧重于治愈概率,并提议一个两步程序,以便在样本大小不大的情况下,根据最大可能性估计器的性能改进治疗概率和未治愈对象的存活率; 新方法的基础是先建造非参数估计器,然后将其投射到理想的参数类; 我们调查由此得出的估计器的理论特性,并通过对逻辑-毒性模型进行广泛的模拟研究,表明它比现有方法高。 这种方法的实际使用通过两种数据图示我。